Sarepta Therapeutics

sarepta.com

Sarepta Therapeutics is a global biotechnology company dedicated to engineering precision genetic medicine for rare diseases. The company focuses on developing innovative therapies using gene therapy, RNA technologies, and gene editing, particularly for conditions like Duchenne muscular dystrophy and limb-girdle muscular dystrophy. With a mission to shorten the time from lab to patient, Sarepta is building the world's largest gene therapy manufacturing capacity and rethinking access and reimbursement models for its treatments. The company is positioned at the forefront of genetic medicine, aiming to transform the lives of patients affected by rare diseases.